Duchenne Muscular Dystrophy Clinical Trials in St Louis, Missouri

4 studies are recruiting for duchenne muscular dystrophy in St Louis, Missouri right now. Each one is listed on ClinicalTrials.gov, the public registry the research teams themselves file with. TrialBoost is not a doctor, a research site, or a study sponsor: the research team decides who takes part.

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Studies now recruiting

1. Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients

   Phase 2a trial of SAT-3247 in ambulatory DMD patients aged ≥ 7 and < 10 years. The trial has two parts. In Part 1, the trial will study two doses of SAT-3247 in a randomized, double-blind, placebo-controlled weekday regimen for 12 weeks to determine the optimal dose, safety, tolerability, and preli…

   Stage

   Phase 2

   Ages

   7 to 9

   Site

   Washington University, St Louis, Missouri

   Locations

   21 in total

   Run by

   Satellos Bioscience, Inc.

   See if you can join NCT07287189 on ClinicalTrials.gov

2. A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

   Cohort 8 (non-ambulatory participants) is currently enrolling new participants. Enrollment for Cohorts 1 through 7 has been completed. This is an open-label gene transfer therapy study evaluating the safety of and expression from delandistrogene moxeparvovec in participants with Duchenne Muscular D…

   Stage

   Phase 1

   Ages

   2 and older

   Site

   Washington University in St. Louis, St Louis, Missouri

   Locations

   12 in total

   Run by

   Sarepta Therapeutics, Inc.

   See if you can join NCT04626674 on ClinicalTrials.gov

3. A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

   This is a multicenter, open-label, non-randomized study to investigate the safety, tolerability, and efficacy of a single intravenous (IV) infusion of SGT-003 in participants with Duchenne muscular dystrophy. There will be 5 cohorts in this study. Cohort 1 will include participants 4 to < 7 years o…

   Stage

   Phase 1

   Ages

   0 to 17

   Site

   Washington University in St. Louis, St Louis, Missouri

   Locations

   15 in total

   Run by

   Solid Biosciences Inc.

   See if you can join NCT06138639 on ClinicalTrials.gov

4. Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study

   This is an open label, long-term safety, tolerability, and efficacy study of GIVINOSTAT in all DMD (Duchenne's muscular dystrophy) patients who have been previously treated in one of the GIVINOSTAT studies.

   Stage

   Phase 2

   Ages

   7 and older

   Site

   Washington University School of Medicine in St Louis Department of Neurology 660 S.Euclid Avenue, Campus Box 8111, St Louis, Missouri

   Locations

   39 in total

   Run by

   Italfarmaco

   See if you can join NCT03373968 on ClinicalTrials.gov