Duchenne Muscular Dystrophy Clinical Trials in Gainesville, Florida

6 studies are recruiting for duchenne muscular dystrophy in Gainesville, Florida right now. Each one is listed on ClinicalTrials.gov, the public registry the research teams themselves file with. TrialBoost is not a doctor, a research site, or a study sponsor: the research team decides who takes part.

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Studies now recruiting

1. A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

   Cohort 8 (non-ambulatory participants) is currently enrolling new participants. Enrollment for Cohorts 1 through 7 has been completed. This is an open-label gene transfer therapy study evaluating the safety of and expression from delandistrogene moxeparvovec in participants with Duchenne Muscular D…

   Stage

   Phase 1

   Ages

   2 and older

   Site

   University of Florida, Gainesville, Florida

   Locations

   12 in total

   Run by

   Sarepta Therapeutics, Inc.

   See if you can join NCT04626674 on ClinicalTrials.gov

2. Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy Patients

   This pilot study will investigate the potential efficacy of VM100, a nutritional supplement specifically formulated for patients with DMD, on quality of life and physical symptoms. Twenty patients (aged 8 an over) will be enrolled to undergo a 10-week placebo-controlled intervention with VM100. Out…

   Stage

   Not phased

   Ages

   6 and older

   Site

   University of Florida, Gainesville, Florida

   Run by

   University of Florida

   See if you can join NCT07766980 on ClinicalTrials.gov

3. Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

   The goal of this study is to collect additional information on the safety of long-term treatment with AGAMREE® and to explore long-term clinical impact of AGAMREE® on quality of life, as assessed by standardized patient-reported outcome measures (QoL questionnaires) in male patients aged 2 years an…

   Stage

   Not phased

   Ages

   2 and older

   Site

   University of Florida Clinical and Translational Science Institue, Gainesville, Florida

   Locations

   33 in total

   Run by

   Catalyst Pharmaceuticals, Inc.

   See if you can join NCT06564974 on ClinicalTrials.gov

4. Vasodilator and Exercise Study for DMD (VASO-REx)

   Examining two strategies as potential adjuvant therapies for Duchenne muscular dystrophy (DMD); aerobic exercise training (to induce adaptations in skeletal muscle and improve cardiovascular health) and tadalafil, an FDA-approved vasodilator (to optimize blood flow and muscle perfusion which is imp…

   Stage

   Phase 2

   Ages

   6 and older

   Site

   University of Florida Clinical and Translational Research Building, Gainesville, Florida

   Run by

   University of Florida

   See if you can join NCT06290713 on ClinicalTrials.gov

5. Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study

   This is an open label, long-term safety, tolerability, and efficacy study of GIVINOSTAT in all DMD (Duchenne's muscular dystrophy) patients who have been previously treated in one of the GIVINOSTAT studies.

   Stage

   Phase 2

   Ages

   7 and older

   Site

   Child Health Research Institute, Gainesville, Florida

   Locations

   39 in total

   Run by

   Italfarmaco

   See if you can join NCT03373968 on ClinicalTrials.gov

6. Magnetic Resonance Imaging and Biomarkers for Muscular Dystrophy

   The purpose of this research study is to determine the potential of magnetic resonance imaging, spectroscopy, and whole body imaging to monitor disease progression and to serve as an objective outcome measure for clinical trials in Muscular Dystrophy (MD). The investigators will compare the muscles…

   Stage

   Not phased

   Ages

   5 to 62

   Site

   University of Florida, Gainesville, Florida

   Locations

   3 in total

   Run by

   University of Florida

   See if you can join NCT01484678 on ClinicalTrials.gov